The FDA accepted uniQure's BLA for its Huntington's disease gene therapy and scheduled a May 1, 2027 PDUFA date, with an advisory committee expected.
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Democratic gains in the midterms hand the party power to push back on the Trump administration's health care agenda and set committee leadership.
Historical data and analysts suggest the sector outperforms after midterms, with Democrats focused on priorities other than drug pricing.
The federal lawsuit claims the company concealed safety concerns tied to its drug Rezdiffra.
The layoffs come as the company ends development of two rare disease drugs following a failed trial.
The setback hits a form of muscular dystrophy that currently lacks approved treatments.
The death in rural northern New York highlights resurgent measles transmission amid slipping vaccination rates.
The close advisory vote could affect availability of compounded peptide therapies, with regulators weighing next steps.
Compass has been seen as a frontrunner to win the first psychedelic drug approval, though a nonprofit rival may make the race tight.
Gamida Cell's parent will serve as lead bidder in a court-supervised auction after Karyopharm negotiated a forbearance deal on debt payments.
The think tank urged seniors to shop carefully during open enrollment given wide variation in plan costs.
On an earnings call, Vertex expressed conviction in the coming launch of povetacicept, viewed as important to its future.
It is the first such death this year in the US and the third linked to the ongoing outbreak.
The guidance sets expectations for potency testing in cell and gene therapy development.
The administration will survey key pharmaceutical production components to identify domestic supply chain gaps.
The letter from trial investigators precedes a regulatory decision on the Duchenne muscular dystrophy therapy.
The approval covers a generic version of a groundbreaking HIV prevention medicine, alongside Lonza's purchase of US facilities.
Before Democrats take control, Congress must fund expiring health care programs and confirm HHS nominees.
Democrats gained both chambers and doctors and scientists won key seats.